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Pembrolizumab (MK-3475)

Memorial Sloan Kettering Cancer Center · Phase 3 active Small molecule Under review

Pembrolizumab (MK-3475) is a PD-1 inhibitor Small molecule drug developed by Memorial Sloan Kettering Cancer Center. It is currently in Phase 3 development for Metastatic melanoma, Non-small cell lung cancer (NSCLC), Head and neck squamous cell carcinoma. Also known as: KEYTRUDA®, MK-3475, Keytruda.

Pembrolizumab is a monoclonal antibody that blocks PD-1 on T cells, allowing the immune system to recognize and attack cancer cells.

Pembrolizumab is an antibody that inhibits the programmed cell death protein 1 (PD-1), a protein involved in the regulation of the immune system. It is used to treat various types of cancer, including gastric cancer, gastroesophageal junction cancer, sarcoma, and gastroesophageal adenocarcinoma.

Likelihood of approval
61.3% vs 58.3% industry baseline
If approved by FDA: likely 2028–2030
Steps remaining: NDA/BLA submission
Confidence: High
Why this estimate
  • Baseline phase 3 → approval rate +58.3pp
    Industry-wide phase 3 drugs reach approval ~58.3% of the time (BIO/Informa 2023 industry benchmark across all therapeutic areas).
  • Oncology Phase 3 boost +3.0pp
    Oncology Phase 3 trials have higher approval rates (~61%) than the cross-industry average due to clearer endpoints and FDA oncology pathway.
Predicted approval windows by jurisdiction (conditional on FDA approval)
Regulator Country Likely year Lag vs FDA
FDA US 2028–2030
EMA EU 2029–2031 +0.7 yr
MHRA GB 2029–2031 +0.7 yr
Health Canada CA 2029–2032 +0.9 yr
TGA AU 2029–2032 +1.2 yr
PMDA JP 2029–2032 +1.5 yr
NMPA CN 2030–2033 +2.3 yr
MFDS KR 2029–2032 +1.4 yr
CDSCO IN 2029–2033 +1.8 yr
ANVISA BR 2030–2033 +2.3 yr

Hover any row for the lag rationale. Lag estimates are reduced when the drug has FDA Breakthrough or EMA PRIME designation (sponsors file globally in parallel).

Estimate based on the BIO/Informa industry phase transition rates plus per-drug modifiers for therapeutic area, sponsor type, FDA designations, mechanism, and trial design. Per-jurisdiction lags from Tufts CSDD international approval studies. Not investment, clinical or regulatory advice. Methodology: /methodology#likelihood.

At a glance

Generic namePembrolizumab (MK-3475)
Also known asKEYTRUDA®, MK-3475, Keytruda
SponsorMemorial Sloan Kettering Cancer Center
Drug classPD-1 inhibitor
TargetPD-1
ModalitySmall molecule
Therapeutic areaOncology
PhasePhase 3

Mechanism of action

Pembrolizumab binds to programmed death receptor 1 (PD-1) on T lymphocytes, preventing interaction with its ligands PD-L1 and PD-L2 on tumor cells. This blockade releases the 'brakes' on anti-tumor immunity, restoring T cell proliferation, activation, and cytotoxic function. By reinvigorating exhausted T cells, pembrolizumab enables durable anti-tumor responses.

Approved indications

Common side effects

Key clinical trials

Primary sources

Every claim on this page is sourced from regulatory or scientific primary sources. See our editorial policy for full methodology.

SourceUsed for
ClinicalTrials.govTrial enrolment, design, endpoints, results

Competitive intelligence

For the full competitive landscape — auto-detected comparators, recent regulatory actions across the set, upcoming PDUFA, patent timeline, sponsor landscape:

Frequently asked questions about Pembrolizumab (MK-3475)

What is Pembrolizumab (MK-3475)?

Pembrolizumab (MK-3475) is a PD-1 inhibitor drug developed by Memorial Sloan Kettering Cancer Center, indicated for Metastatic melanoma, Non-small cell lung cancer (NSCLC), Head and neck squamous cell carcinoma.

How does Pembrolizumab (MK-3475) work?

Pembrolizumab is a monoclonal antibody that blocks PD-1 on T cells, allowing the immune system to recognize and attack cancer cells.

What is Pembrolizumab (MK-3475) used for?

Pembrolizumab (MK-3475) is indicated for Metastatic melanoma, Non-small cell lung cancer (NSCLC), Head and neck squamous cell carcinoma, Hodgkin lymphoma, Urothelial carcinoma.

Who makes Pembrolizumab (MK-3475)?

Pembrolizumab (MK-3475) is developed by Memorial Sloan Kettering Cancer Center (see full Memorial Sloan Kettering Cancer Center pipeline at /company/memorial-sloan-kettering-cancer-center).

Is Pembrolizumab (MK-3475) also known as anything else?

Pembrolizumab (MK-3475) is also known as KEYTRUDA®, MK-3475, Keytruda.

What drug class is Pembrolizumab (MK-3475) in?

Pembrolizumab (MK-3475) belongs to the PD-1 inhibitor class. See all PD-1 inhibitor drugs at /class/pd-1-inhibitor.

What development phase is Pembrolizumab (MK-3475) in?

Pembrolizumab (MK-3475) is in Phase 3.

What are the side effects of Pembrolizumab (MK-3475)?

Common side effects of Pembrolizumab (MK-3475) include Fatigue, Decreased appetite, Nausea, Diarrhea, Immune-related pneumonitis, Immune-related hepatitis.

What does Pembrolizumab (MK-3475) target?

Pembrolizumab (MK-3475) targets PD-1 and is a PD-1 inhibitor.

Related

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing