EMA — authorised 17 July 2025
- Application: EMEA/H/C/006460
- Marketing authorisation holder: Merck Europe B.V.
- Local brand name: Ezmekly
- Indication: Ezmekly as monotherapy is indicated for the treatment of symptomatic, inoperable plexiform neurofibromas (PN) in paediatric and adult patients with neurofibromatosis type 1 (NF1) aged 2 years and above.
- Pathway: conditional, orphan
- Status: approved
The European Medicines Agency (EMA) approved Ezmekly (MIRDAMETINIB) for the treatment of symptomatic, inoperable plexiform neurofibromas (PN) in patients with neurofibromatosis type 1 (NF1). This approval was granted on 17 July 2025. Ezmekly is indicated for patients aged 2 years and above, including both paediatric and adult patients. The marketing authorisation was granted through the conditional, orphan drug pathway.