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ION363

Ionis Pharmaceuticals, Inc. · Phase 3 active Small molecule

ION363 is an antisense oligonucleotide that reduces production of apolipoprotein C-III (apoC-III), a protein that impairs triglyceride clearance and increases cardiovascular risk.

ION363 is an antisense oligonucleotide that reduces production of apolipoprotein C-III (apoC-III), a protein that impairs triglyceride clearance and increases cardiovascular risk. Used for Hypertriglyceridemia in patients at high cardiovascular risk.

At a glance

Generic nameION363
SponsorIonis Pharmaceuticals, Inc.
Drug classAntisense oligonucleotide
TargetAPOC3 mRNA
ModalitySmall molecule
Therapeutic areaCardiovascular
PhasePhase 3

Mechanism of action

By inhibiting apoC-III expression through antisense technology, ION363 lowers triglyceride levels and improves lipid metabolism. This mechanism addresses a key driver of hypertriglyceridemia and may reduce cardiovascular events in patients with elevated triglycerides despite statin therapy.

Approved indications

Common side effects

Key clinical trials

Primary sources

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SourceUsed for
ClinicalTrials.govTrial enrolment, design, endpoints, results

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