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HYCAMTIN, oral capsules

GlaxoSmithKline · Phase 3 active Small molecule

Topotecan inhibits topoisomerase I, an enzyme required for DNA replication, causing DNA damage and cell death in rapidly dividing cancer cells.

Topotecan inhibits topoisomerase I, an enzyme required for DNA replication, causing DNA damage and cell death in rapidly dividing cancer cells. Used for Small cell lung cancer (SCLC), relapsed or refractory, Ovarian cancer, relapsed, Cervical cancer.

At a glance

Generic nameHYCAMTIN, oral capsules
Also known asHYCAMTIN, oral capsules
SponsorGlaxoSmithKline
Drug classTopoisomerase I inhibitor
TargetTopoisomerase I
ModalitySmall molecule
Therapeutic areaOncology
PhasePhase 3

Mechanism of action

Topotecan binds to and stabilizes the topoisomerase I-DNA complex, preventing the enzyme from completing its catalytic cycle and leading to accumulation of DNA breaks. This mechanism is particularly effective against cancer cells with high replication rates. The oral capsule formulation allows for convenient at-home administration compared to intravenous alternatives.

Approved indications

Common side effects

Key clinical trials

Primary sources

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SourceUsed for
ClinicalTrials.govTrial enrolment, design, endpoints, results

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