Last reviewed · How we verify

GLA5PR GLARS-NF1

Daewon Pharmaceutical Co., Ltd. · Phase 3 active Small molecule

GLA5PR GLARS-NF1 is a glutaminyl-tRNA synthetase (GlnRS) inhibitor designed to selectively target and inhibit neurofibromatosis type 1 (NF1) mutant cells.

GLA5PR GLARS-NF1 is a glutaminyl-tRNA synthetase (GlnRS) inhibitor designed to selectively target and inhibit neurofibromatosis type 1 (NF1) mutant cells. Used for Neurofibromatosis type 1 (NF1)-associated malignancies, NF1-associated plexiform neurofibromas.

At a glance

Generic nameGLA5PR GLARS-NF1
Also known asplacebo (for GLA5PR GLARS-NF1)
SponsorDaewon Pharmaceutical Co., Ltd.
Drug classGlutaminyl-tRNA synthetase inhibitor
TargetGLARS (Glutaminyl-tRNA synthetase)
ModalitySmall molecule
Therapeutic areaOncology
PhasePhase 3

Mechanism of action

The drug exploits a synthetic lethal interaction where NF1-deficient cells become dependent on glutaminyl-tRNA synthetase for survival. By inhibiting this enzyme, GLA5PR GLARS-NF1 selectively kills NF1-mutant tumor cells while sparing normal cells, providing a targeted approach to NF1-associated malignancies.

Approved indications

Common side effects

No common side effects on file.

Key clinical trials

Primary sources

Every claim on this page is sourced from regulatory or scientific primary sources. See our editorial policy for full methodology.

SourceUsed for
ClinicalTrials.govTrial enrolment, design, endpoints, results

Competitive intelligence

For the full competitive landscape — auto-detected comparators, recent regulatory actions across the set, upcoming PDUFA, patent timeline, sponsor landscape: