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GF-001001-00

Ferrer Internacional S.A. · Phase 2 active Small molecule

GF-001001-00 is a NS5A inhibitor Small molecule drug developed by Ferrer Internacional S.A.. It is currently in Phase 2 development for Chronic hepatitis C, Hepatitis C virus infection.

GF-001001-00 is a small molecule that targets the HCV NS5A protein.

GF-001001-00 is a small molecule that targets the HCV NS5A protein. Used for Chronic hepatitis C, Hepatitis C virus infection.

Likelihood of approval
17.3% vs 15.3% industry baseline
If approved by FDA: likely 2031–2034
Steps remaining: Phase 3 → NDA/BLA submission
Confidence: Medium
Why this estimate
  • Baseline phase 2 → approval rate +15.3pp
    Industry-wide phase 2 drugs reach approval ~15.3% of the time (BIO/Informa 2023 industry benchmark across all therapeutic areas).
  • Anti-infectives pathway favourability +2.0pp
    Microbiological endpoints + non-inferiority designs raise approval rates above baseline.
Predicted approval windows by jurisdiction (conditional on FDA approval)
Regulator Country Likely year Lag vs FDA
FDA US 2031–2034
EMA EU 2032–2035 +0.7 yr
MHRA GB 2032–2035 +0.7 yr
Health Canada CA 2032–2036 +0.9 yr
TGA AU 2032–2036 +1.2 yr
PMDA JP 2032–2036 +1.5 yr
NMPA CN 2033–2037 +2.3 yr
MFDS KR 2032–2036 +1.4 yr
CDSCO IN 2032–2037 +1.8 yr
ANVISA BR 2033–2037 +2.3 yr

Hover any row for the lag rationale. Lag estimates are reduced when the drug has FDA Breakthrough or EMA PRIME designation (sponsors file globally in parallel).

Estimate based on the BIO/Informa industry phase transition rates plus per-drug modifiers for therapeutic area, sponsor type, FDA designations, mechanism, and trial design. Per-jurisdiction lags from Tufts CSDD international approval studies. Not investment, clinical or regulatory advice. Methodology: /methodology#likelihood.

At a glance

Generic nameGF-001001-00
SponsorFerrer Internacional S.A.
Drug classNS5A inhibitor
TargetHCV NS5A
ModalitySmall molecule
Therapeutic areaInfectious Diseases
PhasePhase 2

Mechanism of action

GF-001001-00 works by binding to the NS5A protein of the hepatitis C virus, which is essential for viral replication. This binding inhibits the NS5A protein's function, ultimately leading to the reduction of viral load in infected cells.

Approved indications

Common side effects

Key clinical trials

Primary sources

Every claim on this page is sourced from regulatory or scientific primary sources. See our editorial policy for full methodology.

SourceUsed for
ClinicalTrials.govTrial enrolment, design, endpoints, results

Competitive intelligence

For the full competitive landscape — auto-detected comparators, recent regulatory actions across the set, upcoming PDUFA, patent timeline, sponsor landscape:

Frequently asked questions about GF-001001-00

What is GF-001001-00?

GF-001001-00 is a NS5A inhibitor drug developed by Ferrer Internacional S.A., indicated for Chronic hepatitis C, Hepatitis C virus infection.

How does GF-001001-00 work?

GF-001001-00 is a small molecule that targets the HCV NS5A protein.

What is GF-001001-00 used for?

GF-001001-00 is indicated for Chronic hepatitis C, Hepatitis C virus infection.

Who makes GF-001001-00?

GF-001001-00 is developed by Ferrer Internacional S.A. (see full Ferrer Internacional S.A. pipeline at /company/ferrer-internacional-s-a).

What drug class is GF-001001-00 in?

GF-001001-00 belongs to the NS5A inhibitor class. See all NS5A inhibitor drugs at /class/ns5a-inhibitor.

What development phase is GF-001001-00 in?

GF-001001-00 is in Phase 2.

What are the side effects of GF-001001-00?

Common side effects of GF-001001-00 include Fatigue, Headache, Nausea.

What does GF-001001-00 target?

GF-001001-00 targets HCV NS5A and is a NS5A inhibitor.

Related

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing