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Etavopivat Tablets Low dose

Forma Therapeutics, Inc. · Phase 3 active Small molecule

Etavopivat activates the KCNQ1 potassium channel to increase fetal hemoglobin (HbF) production in red blood cells.

Etavopivat activates the KCNQ1 potassium channel to increase fetal hemoglobin (HbF) production in red blood cells. Used for Sickle cell disease.

At a glance

Generic nameEtavopivat Tablets Low dose
Also known asFT-4202
SponsorForma Therapeutics, Inc.
Drug classKCNQ1 potassium channel activator
TargetKCNQ1
ModalitySmall molecule
Therapeutic areaHematology/Oncology
PhasePhase 3

Mechanism of action

Etavopivat is a KCNQ1 potassium channel activator that promotes the differentiation of erythroid progenitor cells toward fetal hemoglobin-producing cells. By increasing HbF levels, the drug reduces sickling and hemolysis in patients with sickle cell disease, thereby reducing vaso-occlusive crises and other complications associated with the disease.

Approved indications

Common side effects

Key clinical trials

Primary sources

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SourceUsed for
ClinicalTrials.govTrial enrolment, design, endpoints, results

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