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doxercalciferol capsules, Hectorol® capsules

Genzyme, a Sanofi Company · FDA-approved active Small molecule

Doxercalciferol is a vitamin D analog that activates the vitamin D receptor to regulate calcium and phosphate metabolism and suppress parathyroid hormone secretion.

Doxercalciferol is a vitamin D analog that activates the vitamin D receptor to regulate calcium and phosphate metabolism and suppress parathyroid hormone secretion. Used for Secondary hyperparathyroidism in patients with chronic kidney disease on dialysis, Secondary hyperparathyroidism in patients with stage 3 or 4 chronic kidney disease not on dialysis.

At a glance

Generic namedoxercalciferol capsules, Hectorol® capsules
SponsorGenzyme, a Sanofi Company
Drug classVitamin D analog
TargetVitamin D receptor (VDR)
ModalitySmall molecule
Therapeutic areaEndocrinology / Nephrology
PhaseFDA-approved

Mechanism of action

Doxercalciferol is a prodrug that is converted in the body to the active metabolite 1,25-dihydroxyvitamin D2, which binds to and activates the vitamin D receptor (VDR) in target tissues. This activation regulates intestinal calcium and phosphate absorption, bone mineralization, and suppresses parathyroid hormone (PTH) production, making it effective for treating secondary hyperparathyroidism in patients with chronic kidney disease.

Approved indications

Common side effects

Key clinical trials

Primary sources

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SourceUsed for
ClinicalTrials.govTrial enrolment, design, endpoints, results

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