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CTAP101 Capsules

OPKO Health, Inc. · Phase 3 active Small molecule

CTAP101 is a capsule formulation of calcitriol (active vitamin D) that enhances calcium absorption and regulates calcium-phosphate metabolism.

CTAP101 is a capsule formulation of calcitriol (active vitamin D) that enhances calcium absorption and regulates calcium-phosphate metabolism. Used for Secondary hyperparathyroidism in patients with chronic kidney disease, Vitamin D deficiency-related mineral metabolism disorders.

At a glance

Generic nameCTAP101 Capsules
Also known asCalcifediol, calcifediol
SponsorOPKO Health, Inc.
Drug classVitamin D analog
TargetVitamin D receptor (VDR)
ModalitySmall molecule
Therapeutic areaNephrology / Endocrinology
PhasePhase 3

Mechanism of action

Calcitriol is the active metabolite of vitamin D that binds to the vitamin D receptor (VDR) in intestinal epithelial cells and bone, promoting calcium and phosphate absorption and homeostasis. This formulation is designed to treat secondary hyperparathyroidism and related mineral metabolism disorders in patients with chronic kidney disease or other conditions causing vitamin D deficiency.

Approved indications

Common side effects

Key clinical trials

Primary sources

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SourceUsed for
ClinicalTrials.govTrial enrolment, design, endpoints, results