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CGRP mAbs and onabotulinumtoxin A

Oslo University Hospital · Phase 3 active Small molecule

This combination blocks calcitonin gene-related peptide (CGRP) signaling via monoclonal antibodies while simultaneously inhibiting acetylcholine release at the neuromuscular junction via onabotulinumtoxin A to reduce migraine frequency and severity.

This combination blocks calcitonin gene-related peptide (CGRP) signaling via monoclonal antibodies while simultaneously inhibiting acetylcholine release at the neuromuscular junction via onabotulinumtoxin A to reduce migraine frequency and severity. Used for Chronic migraine (phase 3 combination study).

At a glance

Generic nameCGRP mAbs and onabotulinumtoxin A
SponsorOslo University Hospital
Drug classMonoclonal antibody + neurotoxin combination
TargetCGRP/CGRP receptor and acetylcholine (via SNARE complex inhibition)
ModalitySmall molecule
Therapeutic areaNeurology
PhasePhase 3

Mechanism of action

CGRP mAbs bind to CGRP or its receptor to prevent neuropeptide-mediated vasodilation and neurogenic inflammation implicated in migraine pathogenesis. OnabotulinumtoxinA blocks acetylcholine release at motor endplates, reducing muscle tension and potentially modulating pain signaling in chronic migraine. The combination targets complementary pathways in migraine biology.

Approved indications

Common side effects

Key clinical trials

Primary sources

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SourceUsed for
ClinicalTrials.govTrial enrolment, design, endpoints, results