Last reviewed · How we verify

CG400549

CrystalGenomics, Inc. · Phase 2 active Small molecule

CG400549 is a selective inhibitor of histone deacetylase 6 (HDAC6) that promotes the degradation of misfolded proteins and modulates immune responses.

CG400549 is a selective inhibitor of histone deacetylase 6 (HDAC6) that promotes the degradation of misfolded proteins and modulates immune responses. Used for Multiple myeloma, Peripheral T-cell lymphoma.

At a glance

Generic nameCG400549
Also known asCohort 3
SponsorCrystalGenomics, Inc.
Drug classHDAC6 inhibitor
TargetHDAC6
ModalitySmall molecule
Therapeutic areaOncology, Neurology
PhasePhase 2

Mechanism of action

HDAC6 inhibition leads to accumulation of acetylated alpha-tubulin and aggresome formation, which enhances the clearance of protein aggregates implicated in neurodegenerative diseases. Additionally, HDAC6 inhibition can modulate T-cell function and enhance anti-tumor immunity, making it relevant for both neurological and oncological indications.

Approved indications

Common side effects

Key clinical trials

Primary sources

Every claim on this page is sourced from regulatory or scientific primary sources. See our editorial policy for full methodology.

SourceUsed for
ClinicalTrials.govTrial enrolment, design, endpoints, results