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Bortezomib, Melphalan, Prednisone, Thalidomide

Fondazione EMN Italy Onlus · Phase 3 active Small molecule

This combination regimen targets multiple pathways in multiple myeloma by inhibiting proteasome function, inducing DNA damage, suppressing TNF-α, and promoting cereblon-mediated protein degradation.

This combination regimen targets multiple pathways in multiple myeloma by inhibiting proteasome function, inducing DNA damage, suppressing TNF-α, and promoting cereblon-mediated protein degradation. Used for Multiple myeloma (newly diagnosed or relapsed/refractory).

At a glance

Generic nameBortezomib, Melphalan, Prednisone, Thalidomide
Also known asBortezomib, Velcade, Thalidomide
SponsorFondazione EMN Italy Onlus
Drug classCombination chemotherapy and immunomodulatory therapy
TargetProteasome (bortezomib), DNA (melphalan), glucocorticoid receptor (prednisone), cereblon (thalidomide)
ModalitySmall molecule
Therapeutic areaOncology
PhasePhase 3

Mechanism of action

Bortezomib is a proteasome inhibitor that blocks NF-κB signaling and triggers apoptosis in myeloma cells. Melphalan is an alkylating agent causing DNA damage. Prednisone is a corticosteroid with immunosuppressive and anti-inflammatory effects. Thalidomide is an immunomodulatory agent that enhances cereblon-mediated degradation of IKZF1 and IKZF3, promoting anti-myeloma activity. Together, these agents provide synergistic cytotoxic and immunomodulatory effects.

Approved indications

Common side effects

Key clinical trials

Primary sources

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SourceUsed for
ClinicalTrials.govTrial enrolment, design, endpoints, results

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