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BIO101

Biophytis · Phase 2 active Small molecule

BIO101 is a small molecule targeting the SARM1 protein to prevent mitochondrial dysfunction.

BIO101 is a small molecule targeting the SARM1 protein to prevent mitochondrial dysfunction. Used for Amyotrophic lateral sclerosis (ALS).

At a glance

Generic nameBIO101
Also known asSarconeos (BIO101), 20 hydroxyecdysone (20E)
SponsorBiophytis
Drug classSARM1 inhibitor
TargetSARM1
ModalitySmall molecule
Therapeutic areaNeurology
PhasePhase 2

Mechanism of action

BIO101 works by inhibiting the SARM1 protein, which is involved in the activation of the NAD+ breakdown pathway. This leads to a decrease in the production of toxic aldehydes that cause mitochondrial dysfunction. By preventing mitochondrial dysfunction, BIO101 aims to slow down or halt the progression of various diseases.

Approved indications

Common side effects

Key clinical trials

Primary sources

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SourceUsed for
ClinicalTrials.govTrial enrolment, design, endpoints, results

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