EMA — authorised 29 May 2019
- Application: EMEA/H/C/003691
- Marketing authorisation holder: bluebird bio (Netherlands) B.V.
- Local brand name: Zynteglo
- Indication: Zynteglo is indicated for the treatment of patients 12 years and older with transfusion-dependent β thalassaemia (TDT) who do not have a β0/β0 genotype, for whom haematopoietic stem cell (HSC) transplantation is appropriate but a human leukocyte antigen (HLA)-matched related HSC donor is not available.
- Pathway: accelerated assessment, conditional, ATMP, PRIME
- Status: withdrawn