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AXS-02

Axsome Therapeutics, Inc. · Phase 3 active Small molecule

AXS-02 is a combination of dextromethorphan and quinidine that enhances NMDA receptor antagonism and sigma-1 receptor modulation to reduce neuropathic pain.

AXS-02 is a combination of dextromethorphan and quinidine that enhances NMDA receptor antagonism and sigma-1 receptor modulation to reduce neuropathic pain. Used for Neuropathic pain associated with chemotherapy-induced peripheral neuropathy (CIPN), Fibromyalgia.

At a glance

Generic nameAXS-02
SponsorAxsome Therapeutics, Inc.
Drug classNMDA receptor antagonist / Sigma-1 receptor modulator combination
TargetNMDA receptor, Sigma-1 receptor
ModalitySmall molecule
Therapeutic areaNeurology / Pain Management
PhasePhase 3

Mechanism of action

AXS-02 combines dextromethorphan (a dissociative NMDA receptor antagonist) with quinidine (which inhibits dextromethorphan metabolism, increasing its bioavailability and CNS penetration). This combination targets both NMDA receptors and sigma-1 receptors, which are implicated in neuropathic pain signaling. The formulation is designed to provide sustained pain relief in conditions characterized by central sensitization and neuropathic mechanisms.

Approved indications

Common side effects

Key clinical trials

Primary sources

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SourceUsed for
ClinicalTrials.govTrial enrolment, design, endpoints, results