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AraC

University of California, San Diego · FDA-approved active Small molecule

AraC (cytarabine) is a nucleoside analog that inhibits DNA synthesis by being incorporated into DNA and blocking chain elongation.

AraC (cytarabine) is a nucleoside analog that inhibits DNA synthesis by being incorporated into DNA and blocking chain elongation. Used for Acute myeloid leukemia (AML), Acute lymphoblastic leukemia (ALL), Chronic myeloid leukemia (CML) in blast crisis.

At a glance

Generic nameAraC
Also known asCytarabine, Ara-C, Arabinosylcytosine, Cytosar-U, cytosine arabinoside
SponsorUniversity of California, San Diego
Drug classNucleoside analog antimetabolite
TargetDNA polymerase; deoxycytidine kinase
ModalitySmall molecule
Therapeutic areaOncology
PhaseFDA-approved

Mechanism of action

AraC is converted intracellularly to its active triphosphate form, which competes with deoxycytidine triphosphate for incorporation into DNA. Once incorporated, it causes chain termination and prevents further DNA replication, leading to cell death. It is primarily effective against rapidly dividing cells, particularly hematopoietic malignancies.

Approved indications

Common side effects

Key clinical trials

Primary sources

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SourceUsed for
ClinicalTrials.govTrial enrolment, design, endpoints, results