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Abiraterone + Prednisolone/Prednisone

AstraZeneca · Phase 3 active Small molecule

Abiraterone + Prednisolone/Prednisone is a CYP17A1 inhibitor (androgen synthesis inhibitor) + glucocorticoid Small molecule drug developed by AstraZeneca. It is currently in Phase 3 development for Metastatic castration-resistant prostate cancer (mCRPC), High-risk metastatic hormone-sensitive prostate cancer (mHSPC).

Abiraterone inhibits CYP17A1 to block androgen synthesis, while prednisolone/prednisone suppresses ACTH-driven adrenal compensation and provides anti-inflammatory effects.

Abiraterone inhibits CYP17A1 to block androgen synthesis, while prednisolone/prednisone suppresses ACTH-driven adrenal compensation and provides anti-inflammatory effects. Used for Metastatic castration-resistant prostate cancer (mCRPC), High-risk metastatic hormone-sensitive prostate cancer (mHSPC).

At a glance

Generic nameAbiraterone + Prednisolone/Prednisone
SponsorAstraZeneca
Drug classCYP17A1 inhibitor (androgen synthesis inhibitor) + glucocorticoid
TargetCYP17A1 (17α-hydroxylase/17,20-lyase)
ModalitySmall molecule
Therapeutic areaOncology
PhasePhase 3

Mechanism of action

Abiraterone acetate is a selective inhibitor of 17α-hydroxylase/17,20-lyase (CYP17A1), a key enzyme in androgen biosynthesis in the testes and adrenal glands. By blocking this enzyme, abiraterone reduces circulating testosterone and other androgens, which are critical for castration-resistant prostate cancer (CRPC) cell growth. Prednisolone or prednisone is co-administered to suppress compensatory ACTH-driven adrenal androgen production and to mitigate mineralocorticoid excess caused by shunting of steroid precursors.

Approved indications

Common side effects

Key clinical trials

Primary sources

Every claim on this page is sourced from regulatory or scientific primary sources. See our editorial policy for full methodology.

SourceUsed for
ClinicalTrials.govTrial enrolment, design, endpoints, results

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Frequently asked questions about Abiraterone + Prednisolone/Prednisone

What is Abiraterone + Prednisolone/Prednisone?

Abiraterone + Prednisolone/Prednisone is a CYP17A1 inhibitor (androgen synthesis inhibitor) + glucocorticoid drug developed by AstraZeneca, indicated for Metastatic castration-resistant prostate cancer (mCRPC), High-risk metastatic hormone-sensitive prostate cancer (mHSPC).

How does Abiraterone + Prednisolone/Prednisone work?

Abiraterone inhibits CYP17A1 to block androgen synthesis, while prednisolone/prednisone suppresses ACTH-driven adrenal compensation and provides anti-inflammatory effects.

What is Abiraterone + Prednisolone/Prednisone used for?

Abiraterone + Prednisolone/Prednisone is indicated for Metastatic castration-resistant prostate cancer (mCRPC), High-risk metastatic hormone-sensitive prostate cancer (mHSPC).

Who makes Abiraterone + Prednisolone/Prednisone?

Abiraterone + Prednisolone/Prednisone is developed by AstraZeneca (see full AstraZeneca pipeline at /company/astrazeneca).

What drug class is Abiraterone + Prednisolone/Prednisone in?

Abiraterone + Prednisolone/Prednisone belongs to the CYP17A1 inhibitor (androgen synthesis inhibitor) + glucocorticoid class. See all CYP17A1 inhibitor (androgen synthesis inhibitor) + glucocorticoid drugs at /class/cyp17a1-inhibitor-androgen-synthesis-inhibitor-glucocorticoid.

What development phase is Abiraterone + Prednisolone/Prednisone in?

Abiraterone + Prednisolone/Prednisone is in Phase 3.

What are the side effects of Abiraterone + Prednisolone/Prednisone?

Common side effects of Abiraterone + Prednisolone/Prednisone include Hypertension, Hypokalemia, Fluid retention/edema, Fatigue, Joint pain/arthralgia, Diarrhea.

What does Abiraterone + Prednisolone/Prednisone target?

Abiraterone + Prednisolone/Prednisone targets CYP17A1 (17α-hydroxylase/17,20-lyase) and is a CYP17A1 inhibitor (androgen synthesis inhibitor) + glucocorticoid.

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