EMA — authorised 22 November 2018
- Application: EMEA/H/C/004451
- Marketing authorisation holder: Novartis Europharm Limited
- Local brand name: Luxturna
- Indication: Luxturna is indicated for the treatment of adult and paediatric patients with vision loss due to inherited retinal dystrophy caused by confirmed biallelic RPE65 mutations and who have sufficient viable retinal cells.
- Pathway: orphan, ATMP
- Status: approved