Last reviewed · How we verify
Spinal muscular atrophy
Approved treatments
- Spinraza · Biogen Idec
Spinraza works by binding to a specific genetic sequence to increase production of a protein that helps maintain muscle function. - Zolgensma · Novartis Pharmaceuticals
- Evrysdi · Roche
Evrysdi works by increasing the production of survival motor neuron protein.
Competitive intelligence
For the full treatment-landscape CI brief — marketed leaders side-by-side, pipeline by phase, recent regulatory actions, sponsor landscape:
- Spinal muscular atrophy patent landscape — cliff calendar, originator estates, attackable patents
- Spinal muscular atrophy treatment landscape brief
- Spinal muscular atrophy treatment updates RSS
Frequently asked questions about Spinal muscular atrophy
What drugs treat Spinal muscular atrophy?
Tracked treatments include Spinraza, Zolgensma, Evrysdi.
What is the treatment for Spinal muscular atrophy?
Standard treatment for Spinal muscular atrophy includes Spinraza, Zolgensma, Evrysdi. See the treatment landscape page for first-line, second-line and salvage options.
Related
- Treatment landscape: Spinal muscular atrophy patent cliff · Spinal muscular atrophy CI report
- Treatment: Spinraza · Biogen Idec
- Treatment: Zolgensma · Novartis Pharmaceuticals
- Treatment: Evrysdi · Roche
- All diseases: Browse the disease index · Disease landscape hub
Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing