Last reviewed · How we verify
Pompe disease
Approved treatments
- NEXVIAZYME · GENZYME CORP
- Neogaa · Sanofi
AVALGLUCOSIDASE ALFA breaks down glycogen in lysosomes to treat Pompe disease.
Competitive intelligence
For the full treatment-landscape CI brief — marketed leaders side-by-side, pipeline by phase, recent regulatory actions, sponsor landscape:
- Pompe disease patent landscape — cliff calendar, originator estates, attackable patents
- Pompe disease treatment landscape brief
- Pompe disease treatment updates RSS
Frequently asked questions about Pompe disease
What drugs treat Pompe disease?
Tracked treatments include NEXVIAZYME, Neogaa.
What is the treatment for Pompe disease?
Standard treatment for Pompe disease includes NEXVIAZYME, Neogaa. See the treatment landscape page for first-line, second-line and salvage options.
Related
- Treatment landscape: Pompe disease patent cliff · Pompe disease CI report
- Treatment: NEXVIAZYME · GENZYME CORP
- Treatment: Neogaa · Sanofi
- All diseases: Browse the disease index · Disease landscape hub
Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing