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Amvuttra — Competitive Intelligence Brief
marketed
Small Interfering RNA
transthyretin (TTR) mRNA
Neuroscience
Oligonucleotide
Live · refreshed every 30 min
Target snapshot
Amvuttra (VUTRISIRAN) — Alnylam Pharmaceuticals. Amvuttra works by silencing the production of abnormal TTR protein through RNA interference.
Comparator set (3 drugs)
| Drug | Generic | Sponsor | Phase | Class | Target | Approval / PDUFA |
|---|---|---|---|---|---|---|
| Amvuttra TARGET | VUTRISIRAN | Alnylam Pharmaceuticals | marketed | Small Interfering RNA | transthyretin (TTR) mRNA | 2022-01-01 |
| Onpattro | PATISIRAN | Alnylam Pharmaceuticals | marketed | Small Interfering RNA | transthyretin (TTR) mRNA | 2018-01-01 |
| Onpattro | PATISIRAN SODIUM | Alnylam Pharmaceuticals | marketed | Small Interfering RNA | transthyretin (TTR) mRNA | 2018-01-01 |
| SYL1001 ophthalmic solution | SYL1001 ophthalmic solution | Sylentis, S.A. | phase 3 | siRNA (small interfering RNA) | TGF-β2 (transforming growth factor-beta 2) |
Recent regulatory actions (last 90 days)
Upcoming PDUFA dates (next 180 days)
Patent timeline (forward window)
Sponsor landscape (Small Interfering RNA class)
- Alnylam Pharmaceuticals · 3 drugs in this class
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Cite this brief
Drug Landscape (2026). Amvuttra — Competitive Intelligence Brief. https://druglandscape.com/ci/vutrisiran. Accessed 2026-05-13.
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