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Familial x-linked hypophosphatemic vitamin D refractory rickets — Treatment Landscape & Competitive Intelligence

Familial x-linked hypophosphatemic vitamin D refractory rickets (disease) competitive landscape: 4 marketed treatments tracked, 0 Phase 3 candidates, 0 Phase 2 candidates. Recent regulatory actions and upcoming PDUFA dates across the entire treatment set.

4 marketed 0 Phase 3 0 Phase 2 Live · 30-min refresh

Marketed treatment landscape

Approved drugs treating Familial x-linked hypophosphatemic vitamin D refractory rickets, deduplicated by molecule. See the full disease page for line-of-therapy detail.

DrugGenericSponsorClassTargetLine of therapyFirst approval
Crysvita BUROSUMAB Ultragenyx Pharm Inc FGF23 2018-01-01
Drisdol ERGOCALCIFEROL Esjay Pharma Provitamin D2 Compound [EPC] 25-hydroxyvitamin D-1 alpha hydroxylase, mitochondrial 1941-01-01
CRYSVITA BUROSUMAB-TWZA KYOWA KIRIN Fibroblast growth factor 23
Calciferol Calciferol Department of Medical Services Ministry of Public Health of Thailand Vitamin D 25-hydroxylase, 25-hydroxyvitamin D-1 alpha hydroxylase, mitochondrial, Vitamin D3 receptor

Phase 3 pipeline

No Phase 3 pipeline candidates tracked.

Phase 2 pipeline

No Phase 2 pipeline candidates tracked.

Recent regulatory actions (last 90 days)

No regulatory actions in the last 90 days for this treatment set.

Upcoming PDUFA dates (next 180 days)

No PDUFA dates in the next 180 days for this treatment set.

Sponsor landscape

  1. Department of Medical Services Ministry of Public Health of Thailand · 1 drug in Familial x-linked hypophosphatemic vitamin D refractory rickets
  2. Esjay Pharma · 1 drug in Familial x-linked hypophosphatemic vitamin D refractory rickets
  3. KYOWA KIRIN · 1 drug in Familial x-linked hypophosphatemic vitamin D refractory rickets
  4. Ultragenyx Pharm Inc · 1 drug in Familial x-linked hypophosphatemic vitamin D refractory rickets

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Every new regulatory action, PDUFA date, or trial completion in Familial x-linked hypophosphatemic vitamin D refractory rickets:

Cite this brief

Drug Landscape (2026). Familial x-linked hypophosphatemic vitamin D refractory rickets — Treatment Landscape & Competitive Intelligence Brief. https://druglandscape.com/ci/disease/familial-x-linked-hypophosphatemic-vitamin-d-refractory-rickets. Accessed 2026-06-09.

Related

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing