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AOC 1001 (del-desiran) — Competitive Intelligence Brief
phase 3
Antisense oligonucleotide conjugate
Rare genetic disease
Small molecule
Live · refreshed every 30 min
Target snapshot
AOC 1001 (del-desiran) (AOC 1001 (del-desiran)) — Avidity Biosciences, Inc.. AOC 1001 is an antisense oligonucleotide conjugate that targets and reduces expression of a disease-causing gene through a tissue-directed delivery approach.
Comparator set
| Drug | Generic | Sponsor | Phase | Class | Target | Approval / PDUFA |
|---|---|---|---|---|---|---|
| AOC 1001 (del-desiran) TARGET | AOC 1001 (del-desiran) | Avidity Biosciences, Inc. | phase 3 | Antisense oligonucleotide conjugate |
Recent regulatory actions (last 90 days)
Upcoming PDUFA dates (next 180 days)
Patent timeline (forward window)
Sponsor landscape (Antisense oligonucleotide conjugate class)
- Avidity Biosciences, Inc. · 1 drug in this class
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Cite this brief
Drug Landscape (2026). AOC 1001 (del-desiran) — Competitive Intelligence Brief. https://druglandscape.com/ci/aoc-1001-del-desiran. Accessed 2026-05-18.
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