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ADA gene transfer — Competitive Intelligence Brief
phase 2
ADA gene
Immunology
Biologic
Live · refreshed every 30 min
Target snapshot
ADA gene transfer (ADA gene transfer) — Donald B. Kohn, M.D.. ADA gene transfer involves the introduction of a healthy copy of the ADA gene into a patient's hematopoietic stem cells to treat ADA-SCID.
Comparator set
| Drug | Generic | Sponsor | Phase | Class | Target | Approval / PDUFA |
|---|---|---|---|---|---|---|
| ADA gene transfer TARGET | ADA gene transfer | Donald B. Kohn, M.D. | phase 2 | ADA gene |
Recent regulatory actions (last 90 days)
Upcoming PDUFA dates (next 180 days)
Patent timeline (forward window)
Sponsor landscape
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Cite this brief
Drug Landscape (2026). ADA gene transfer — Competitive Intelligence Brief. https://druglandscape.com/ci/ada-gene-transfer. Accessed 2026-05-16.
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