{"disease":{"id":"wolman-disease","name":"wolman disease"},"drugs":{"marketed":[],"pipeline":[],"offLabel":[],"totalMarketed":0,"totalPipeline":0},"trials":{"data":[{"nct_id":"NCT01633489","title":"Lysosomal Acid Lipase (LAL) Deficiency Registry","phase":"","overall_status":"RECRUITING","enrollment_count":300,"lead_sponsor_name":"Alexion Pharmaceuticals, Inc.","has_results":false},{"nct_id":"NCT05619900","title":"Registry of Patients Diagnosed With Lysosomal Storage Diseases","phase":"","overall_status":"RECRUITING","enrollment_count":250,"lead_sponsor_name":"University of California, San Francisco","has_results":false},{"nct_id":"NCT04792671","title":"Prevalence and Risk Factors of Women Mental Health Disorders","phase":"","overall_status":"UNKNOWN","enrollment_count":200,"lead_sponsor_name":"Assiut University","has_results":false},{"nct_id":"NCT06287658","title":"The Effect of Kegel Exercise and Ba Duan Jin Applications on Premenopausal Women With Urinary Incontinence","phase":"NA","overall_status":"RECRUITING","enrollment_count":60,"lead_sponsor_name":"Ondokuz Mayıs University","has_results":false},{"nct_id":"NCT04652713","title":"Breakfast for Young Women","phase":"NA","overall_status":"COMPLETED","enrollment_count":30,"lead_sponsor_name":"University of Aarhus","has_results":false},{"nct_id":"NCT04532047","title":"PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)","phase":"PHASE1","overall_status":"RECRUITING","enrollment_count":10,"lead_sponsor_name":"University of California, San Francisco","has_results":false},{"nct_id":"NCT01371825","title":"Safety, Tolerability, Efficacy, Pharmacokinetics, and Pharmacodynamics of Sebelipase Alfa in Children With Growth Failure Due to Lysosomal Acid Lipase Deficiency","phase":"PHASE2, PHASE3","overall_status":"COMPLETED","enrollment_count":9,"lead_sponsor_name":"Alexion Pharmaceuticals, Inc.","has_results":true},{"nct_id":"NCT02383641","title":"Biomarker for Wolman Disease (BioWolman)","phase":"","overall_status":"WITHDRAWN","enrollment_count":0,"lead_sponsor_name":"CENTOGENE GmbH Rostock","has_results":false}],"total":8},"guidelines":[],"source":"Drug Landscape verified database"}