{"disease":{"id":"spinal-muscular-atrophy-type-ii","name":"spinal muscular atrophy type ii"},"drugs":{"marketed":[],"pipeline":[],"offLabel":[],"totalMarketed":0,"totalPipeline":0},"trials":{"data":[{"nct_id":"NCT03655223","title":"Early Check: Expanded Screening in Newborns","phase":"","overall_status":"ENROLLING_BY_INVITATION","enrollment_count":30000,"lead_sponsor_name":"RTI International","has_results":false},{"nct_id":"NCT03709784","title":"Spinraza in Adult Spinal Muscular Atrophy","phase":"","overall_status":"ACTIVE_NOT_RECRUITING","enrollment_count":148,"lead_sponsor_name":"Washington University School of Medicine","has_results":false},{"nct_id":"NCT04042025","title":"Long-term Follow-up Study of Patients Receiving Onasemnogene Abeparvovec-xioi","phase":"PHASE3","overall_status":"ACTIVE_NOT_RECRUITING","enrollment_count":85,"lead_sponsor_name":"Novartis Gene Therapies","has_results":false},{"nct_id":"NCT06632730","title":"Therapeutic Management and Use of Resources and Costs of Spinal Muscular Atrophy in Spain","phase":"","overall_status":"COMPLETED","enrollment_count":69,"lead_sponsor_name":"Novartis","has_results":false},{"nct_id":"NCT05839145","title":"Home Monitoring of Adult Patients With SMA: a Pilot Multicenter Validation Study","phase":"NA","overall_status":"UNKNOWN","enrollment_count":60,"lead_sponsor_name":"Institut de Myologie, France","has_results":false},{"nct_id":"NCT06137612","title":"Spinal Cord Gray Matter Imaging in Spinal Muscular Atrophy","phase":"","overall_status":"UNKNOWN","enrollment_count":52,"lead_sponsor_name":"University Hospital, Basel, Switzerland","has_results":false},{"nct_id":"NCT05715749","title":"Body Weight Support Harness System in Spinal Muscular Atrophy","phase":"NA","overall_status":"COMPLETED","enrollment_count":33,"lead_sponsor_name":"Nationwide Children's Hospital","has_results":false},{"nct_id":"NCT05416034","title":"Exoskeleton Impact on the Quality of Life on Patients With Spinal Muscular Atrophy","phase":"NA","overall_status":"COMPLETED","enrollment_count":3,"lead_sponsor_name":"MarsiBionics","has_results":false}],"total":8},"guidelines":[],"source":"Drug Landscape verified database"}