{"disease":{"id":"sickle-cell-hemoglobin-c","name":"sickle cell hemoglobin c"},"drugs":{"marketed":[],"pipeline":[],"offLabel":[],"totalMarketed":0,"totalPipeline":0},"trials":{"data":[{"nct_id":"NCT06831799","title":"ERN-EuroBloodNet Registry on Patients With Rare Red Blood Cell Defects and COVID-19","phase":"","overall_status":"COMPLETED","enrollment_count":684,"lead_sponsor_name":"Hospital Universitari Vall d'Hebron Research Institute","has_results":false},{"nct_id":"NCT04201210","title":"A Trial to Assess Haploidentical T-depleted Stem Cell Transplantation in Patients With SCD","phase":"PHASE2","overall_status":"RECRUITING","enrollment_count":212,"lead_sponsor_name":"University of Regensburg","has_results":false},{"nct_id":"NCT04208529","title":"A Long-term Follow-up Study in Participants Who Received CTX001","phase":"PHASE3","overall_status":"ENROLLING_BY_INVITATION","enrollment_count":160,"lead_sponsor_name":"Vertex Pharmaceuticals Incorporated","has_results":false},{"nct_id":"NCT04691323","title":"The Longitudinal Relationship of HU Adherence to HRQOL, Barriers to Adherence and Habit in SCD.","phase":"NA","overall_status":"ACTIVE_NOT_RECRUITING","enrollment_count":68,"lead_sponsor_name":"Ann & Robert H Lurie Children's Hospital of Chicago","has_results":false},{"nct_id":"NCT04678037","title":"Home-based Assessment of PRO Measures in SCD Using A Smartphone App Platform: A Feasibility Study","phase":"NA","overall_status":"COMPLETED","enrollment_count":40,"lead_sponsor_name":"Ann & Robert H Lurie Children's Hospital of Chicago","has_results":false},{"nct_id":"NCT04688411","title":"An mHealth Strategy to Improve Medication Adherence in Adolescents With Sickle Cell Disease","phase":"NA","overall_status":"RECRUITING","enrollment_count":40,"lead_sponsor_name":"Ann & Robert H Lurie Children's Hospital of Chicago","has_results":false},{"nct_id":"NCT02179359","title":"Hematopoietic Stem Cell Transplant for High Risk Hemoglobinopathies","phase":"NA","overall_status":"TERMINATED","enrollment_count":38,"lead_sponsor_name":"Masonic Cancer Center, University of Minnesota","has_results":false},{"nct_id":"NCT03763656","title":"Pharmacokinetics of Oral Hydroxyurea Solution","phase":"PHASE1, PHASE2","overall_status":"COMPLETED","enrollment_count":33,"lead_sponsor_name":"Nova Laboratories Limited","has_results":true},{"nct_id":"NCT04675645","title":"Adherence to HU and HRQOL in Patients With Sickle Cell Disease: An Intervention Study Using HU-Go App","phase":"NA","overall_status":"COMPLETED","enrollment_count":33,"lead_sponsor_name":"Ann & Robert H Lurie Children's Hospital of Chicago","has_results":false},{"nct_id":"NCT05904093","title":"Study to Evaluate the Safety and Tolerability of Escalating Doses of Fostamatinib in Subjects With Stable Sickle Cell Disease","phase":"PHASE1","overall_status":"RECRUITING","enrollment_count":25,"lead_sponsor_name":"National Heart, Lung, and Blood Institute (NHLBI)","has_results":false},{"nct_id":"NCT05329649","title":"Evaluation of Safety and Efficacy of CTX001 in Pediatric Participants With Severe Sickle Cell Disease (SCD)","phase":"PHASE3","overall_status":"ACTIVE_NOT_RECRUITING","enrollment_count":13,"lead_sponsor_name":"Vertex Pharmaceuticals Incorporated","has_results":false},{"nct_id":"NCT03249831","title":"A Blood Stem Cell Transplant for Sickle Cell Disease","phase":"PHASE1","overall_status":"ACTIVE_NOT_RECRUITING","enrollment_count":3,"lead_sponsor_name":"City of Hope Medical Center","has_results":false}],"total":12},"guidelines":[],"source":"Drug Landscape verified database"}