{"disease":{"id":"shank3-haploinsufficiency","name":"shank3 haploinsufficiency"},"drugs":{"marketed":[],"pipeline":[],"offLabel":[],"totalMarketed":0,"totalPipeline":0},"trials":{"data":[{"nct_id":"NCT07014020","title":"RB001 Gene Therapy Study in Children With SHANK3-related Phelan McDermid Syndrome (PMS)","phase":"NA","overall_status":"RECRUITING","enrollment_count":8,"lead_sponsor_name":"Peking University First Hospital","has_results":false}],"total":1},"guidelines":[],"source":"Drug Landscape verified database"}