{"disease":{"id":"severe-combined-immunodeficiency-due-to-rag1-deficiency","name":"severe combined immunodeficiency due to rag1 deficiency"},"drugs":{"marketed":[],"pipeline":[],"offLabel":[],"totalMarketed":0,"totalPipeline":0},"trials":{"data":[{"nct_id":"NCT03655223","title":"Early Check: Expanded Screening in Newborns","phase":"","overall_status":"ENROLLING_BY_INVITATION","enrollment_count":30000,"lead_sponsor_name":"RTI International","has_results":false},{"nct_id":"NCT04797260","title":"Phase I/II Clinical Trial Stem Cell Gene Therapy in RAG1-Deficient SCID","phase":"NA","overall_status":"RECRUITING","enrollment_count":10,"lead_sponsor_name":"Leiden University Medical Center","has_results":false}],"total":2},"guidelines":[],"source":"Drug Landscape verified database"}