{"disease":{"id":"ryr-1-myopathy","name":"ryr 1 myopathy"},"drugs":{"marketed":[],"pipeline":[],"offLabel":[],"totalMarketed":0,"totalPipeline":0},"trials":{"data":[{"nct_id":"NCT04141670","title":"S 48168 (ARM 210) for the Treatment of RYR1-related Myopathies (RYR1-RM)","phase":"PHASE1","overall_status":"COMPLETED","enrollment_count":7,"lead_sponsor_name":"RyCarma Therapeutics, Inc.","has_results":true}],"total":1},"guidelines":[],"source":"Drug Landscape verified database"}