{"disease":{"id":"pyruvate-dehydrogenase-e2-deficiency","name":"pyruvate dehydrogenase e2 deficiency"},"drugs":{"marketed":[],"pipeline":[],"offLabel":[],"totalMarketed":0,"totalPipeline":0},"trials":{"data":[{"nct_id":"NCT05257005","title":"Natural History Study of Pyruvate Dehydrogenase Deficiency","phase":"","overall_status":"UNKNOWN","enrollment_count":50,"lead_sponsor_name":"Great Ormond Street Hospital for Children NHS Foundation Trust","has_results":false}],"total":1},"guidelines":[],"source":"Drug Landscape verified database"}