{"disease":{"id":"pompe-s-disease-juvenile-onset","name":"pompe s disease juvenile onset"},"drugs":{"marketed":[],"pipeline":[],"offLabel":[],"totalMarketed":0,"totalPipeline":0},"trials":{"data":[{"nct_id":"NCT05083806","title":"MSOT in Pompe Disease","phase":"NA","overall_status":"COMPLETED","enrollment_count":20,"lead_sponsor_name":"University of Erlangen-Nürnberg Medical School","has_results":false},{"nct_id":"NCT04942912","title":"Effect of Enzyme Replacement Therapy in Patients With Juvenile-onset Pompe Disease","phase":"","overall_status":"UNKNOWN","enrollment_count":10,"lead_sponsor_name":"Central Hospital, Nancy, France","has_results":false}],"total":2},"guidelines":[],"source":"Drug Landscape verified database"}