{"disease":{"id":"pearson-syndrome","name":"pearson syndrome"},"drugs":{"marketed":[],"pipeline":[],"offLabel":[],"totalMarketed":0,"totalPipeline":0},"trials":{"data":[{"nct_id":"NCT05029843","title":"SLSMDS Natural History Study","phase":"","overall_status":"UNKNOWN","enrollment_count":30,"lead_sponsor_name":"The Champ Foundation","has_results":false},{"nct_id":"NCT03384420","title":"A Study to Evaluate the Safety and Therapeutic Effects of Transplantation of MNV-BM-BLD in Pediatric Patients With Pearson Syndrome","phase":"PHASE1, PHASE2","overall_status":"COMPLETED","enrollment_count":7,"lead_sponsor_name":"Minovia Therapeutics Ltd.","has_results":false},{"nct_id":"NCT02104336","title":"Phase 2 Study of EPI-743 in Children With Pearson Syndrome","phase":"PHASE2","overall_status":"TERMINATED","enrollment_count":2,"lead_sponsor_name":"Edison Pharmaceuticals Inc","has_results":false}],"total":3},"guidelines":[],"source":"Drug Landscape verified database"}