{"disease":{"id":"paroxysmal-hemoglobinuria-nocturnal","name":"paroxysmal hemoglobinuria nocturnal"},"drugs":{"marketed":[],"pipeline":[],"offLabel":[],"totalMarketed":0,"totalPipeline":0},"trials":{"data":[{"nct_id":"NCT00130000","title":"Eculizumab to Treat Paroxysmal Nocturnal Hemoglobinuria","phase":"PHASE3","overall_status":"COMPLETED","enrollment_count":87,"lead_sponsor_name":"National Heart, Lung, and Blood Institute (NHLBI)","has_results":false},{"nct_id":"NCT03157635","title":"Study to Assess Safety, Efficacy, Pharmacokinetics, and Pharmacodynamics of Crovalimab in Healthy Volunteers and Participants With Paroxysmal Nocturnal Hemoglobinuria","phase":"PHASE1, PHASE2","overall_status":"ACTIVE_NOT_RECRUITING","enrollment_count":59,"lead_sponsor_name":"Hoffmann-La Roche","has_results":false}],"total":2},"guidelines":[],"source":"Drug Landscape verified database"}