{"disease":{"id":"oculopharyngeal-muscular-dystrophy","name":"oculopharyngeal muscular dystrophy"},"drugs":{"marketed":[],"pipeline":[],"offLabel":[],"totalMarketed":0,"totalPipeline":0},"trials":{"data":[{"nct_id":"NCT03161847","title":"Natural History Study of Oculopharyngeal Muscular Dystrophy","phase":"","overall_status":"WITHDRAWN","enrollment_count":0,"lead_sponsor_name":"University of New Mexico","has_results":false},{"nct_id":"NCT04226924","title":"Treatment of Oculopharyngeal Muscular Dystrophy With Trehalose","phase":"PHASE2","overall_status":"WITHDRAWN","enrollment_count":0,"lead_sponsor_name":"Bioblast Pharma Ltd.","has_results":false}],"total":2},"guidelines":[],"source":"Drug Landscape verified database"}