{"disease":{"id":"mucopolysaccharidoses","name":"mucopolysaccharidoses"},"drugs":{"marketed":[],"pipeline":[],"offLabel":[],"totalMarketed":0,"totalPipeline":0},"trials":{"data":[{"nct_id":"NCT03047369","title":"The Myelin Disorders Biorepository Project","phase":"","overall_status":"RECRUITING","enrollment_count":12000,"lead_sponsor_name":"Children's Hospital of Philadelphia","has_results":false},{"nct_id":"NCT02699190","title":"LeukoSEQ: Whole Genome Sequencing as a First-Line Diagnostic Tool for Leukodystrophies","phase":"","overall_status":"COMPLETED","enrollment_count":236,"lead_sponsor_name":"Children's Hospital of Philadelphia","has_results":true},{"nct_id":"NCT05354219","title":"Validation and Reliability of Iris Cameras in Mucopolysaccharidoses","phase":"","overall_status":"UNKNOWN","enrollment_count":60,"lead_sponsor_name":"Manchester University NHS Foundation Trust","has_results":false},{"nct_id":"NCT05063435","title":"Cardiovascular Structure and Function in the Mucopolysaccharidoses","phase":"","overall_status":"ACTIVE_NOT_RECRUITING","enrollment_count":30,"lead_sponsor_name":"Children's Hospital of Orange County","has_results":false},{"nct_id":"NCT04112602","title":"Respiratory Cathepsins, Proteases Inhibitors and Glycosaminoglycans (GAG) in Mucopolysaccharidosis","phase":"","overall_status":"COMPLETED","enrollment_count":27,"lead_sponsor_name":"University Hospital, Tours","has_results":false},{"nct_id":"NCT04637646","title":"Evaluation of Cardiac Affections in Patients With Mucopolysaccharidosis (MPS) in Assuit University Children Hospital (AUCH)","phase":"","overall_status":"UNKNOWN","enrollment_count":25,"lead_sponsor_name":"Assiut University","has_results":false},{"nct_id":"NCT04491747","title":"Assessment of Factors That Affected Respiratory Parameters in Mucopolysaccharidoses Patients","phase":"","overall_status":"COMPLETED","enrollment_count":24,"lead_sponsor_name":"Hacettepe University","has_results":false},{"nct_id":"NCT03632213","title":"Evaluation of Losartan on Cardiovascular Disease in Patients With Mucopolysaccharidoses IV A and VI","phase":"PHASE2","overall_status":"UNKNOWN","enrollment_count":10,"lead_sponsor_name":"Hospital de Clinicas de Porto Alegre","has_results":false}],"total":8},"guidelines":[],"source":"Drug Landscape verified database"}