{"disease":{"id":"mucolipidosis-type-iv","name":"mucolipidosis type iv"},"drugs":{"marketed":[],"pipeline":[],"offLabel":[],"totalMarketed":0,"totalPipeline":0},"trials":{"data":[{"nct_id":"NCT00015782","title":"The Natural History and Pathogenesis of Mucolipidosis Type IV","phase":"","overall_status":"COMPLETED","enrollment_count":30,"lead_sponsor_name":"National Institute of Neurological Disorders and Stroke (NINDS)","has_results":false},{"nct_id":"NCT01067742","title":"The Natural History of Mucolipidosis Type IV","phase":"","overall_status":"TERMINATED","enrollment_count":7,"lead_sponsor_name":"Baylor Research Institute","has_results":false},{"nct_id":"NCT07398872","title":"Safety and Efficacy of AAV9. hMCOLN1co For Patients With Mucolipidosis Type IV","phase":"PHASE1","overall_status":"ENROLLING_BY_INVITATION","enrollment_count":1,"lead_sponsor_name":"The Children's Hospital of Zhejiang University School of Medicine","has_results":false}],"total":3},"guidelines":[],"source":"Drug Landscape verified database"}