{"disease":{"id":"mps-mucopolysaccharidosis","name":"mps mucopolysaccharidosis"},"drugs":{"marketed":[],"pipeline":[],"offLabel":[],"totalMarketed":0,"totalPipeline":0},"trials":{"data":[{"nct_id":"NCT07361536","title":"Cardiac Structure and Function in MPS","phase":"","overall_status":"RECRUITING","enrollment_count":240,"lead_sponsor_name":"Children's Hospital of Orange County","has_results":false},{"nct_id":"NCT03150069","title":"Pregnancy With Morquio Syndrome - What Are Patients' Perspectives and Has ERT Changed Them?","phase":"","overall_status":"COMPLETED","enrollment_count":18,"lead_sponsor_name":"Emory University","has_results":false},{"nct_id":"NCT02432144","title":"A Study of UX003 Recombinant Human Beta-Glucuronidase (rhGUS) Enzyme Replacement Therapy in Subjects With Mucopolysaccharidosis Type 7, Sly Syndrome (MPS 7)","phase":"PHASE3","overall_status":"COMPLETED","enrollment_count":12,"lead_sponsor_name":"Ultragenyx Pharmaceutical Inc","has_results":true},{"nct_id":"NCT03632213","title":"Evaluation of Losartan on Cardiovascular Disease in Patients With Mucopolysaccharidoses IV A and VI","phase":"PHASE2","overall_status":"UNKNOWN","enrollment_count":10,"lead_sponsor_name":"Hospital de Clinicas de Porto Alegre","has_results":false},{"nct_id":"NCT02418455","title":"Study of UX003 Recombinant Human Beta-Glucuronidase (rhGUS) Enzyme Replacement Treatment in Mucopolysaccharidosis Type 7, Sly Syndrome (MPS 7) Patients Less Than 5 Years of Age","phase":"PHASE2","overall_status":"COMPLETED","enrollment_count":8,"lead_sponsor_name":"Ultragenyx Pharmaceutical Inc","has_results":true},{"nct_id":"NCT04976231","title":"MPS II Immunophenotyping","phase":"","overall_status":"TERMINATED","enrollment_count":6,"lead_sponsor_name":"Duke University","has_results":false},{"nct_id":"NCT04088734","title":"Gene Transfer Study of ABO-102 in Patients With Middle and Advanced Phases of MPS IIIA Disease","phase":"PHASE1, PHASE2","overall_status":"TERMINATED","enrollment_count":5,"lead_sponsor_name":"Ultragenyx Pharmaceutical Inc","has_results":true},{"nct_id":"NCT03775174","title":"Expanded Access to Mepsevii","phase":"","overall_status":"AVAILABLE","enrollment_count":null,"lead_sponsor_name":"Ultragenyx Pharmaceutical Inc","has_results":false}],"total":8},"guidelines":[],"source":"Drug Landscape verified database"}