{"disease":{"id":"monocarboxylate-transporter-8-deficiency","name":"monocarboxylate transporter 8 deficiency"},"drugs":{"marketed":[],"pipeline":[],"offLabel":[],"totalMarketed":0,"totalPipeline":0},"trials":{"data":[{"nct_id":"NCT06060197","title":"MCT8 Deficiency Caregiver Study","phase":"","overall_status":"COMPLETED","enrollment_count":21,"lead_sponsor_name":"Rare Thyroid Therapeutics International AB","has_results":false},{"nct_id":"NCT05579327","title":"Withdrawal of Tiratricol Treatment in Males With Monocarboxylate Transporter 8 Deficiency (MCT8 Deficiency)","phase":"PHASE3","overall_status":"COMPLETED","enrollment_count":20,"lead_sponsor_name":"Rare Thyroid Therapeutics International AB","has_results":false},{"nct_id":"NCT05019417","title":"Glycerol-Phenylbutyrate Treatment in Children With MCT Mutation (Allan-Herndon- Dudley Syndrome)","phase":"PHASE2, PHASE3","overall_status":"UNKNOWN","enrollment_count":6,"lead_sponsor_name":"Kaplan Medical Center","has_results":false},{"nct_id":"NCT05911399","title":"Expanded Access Program for Tiratricol in Patients With Monocarboxylate Transporter 8 Deficiency","phase":"","overall_status":"AVAILABLE","enrollment_count":null,"lead_sponsor_name":"Rare Thyroid Therapeutics International AB","has_results":false}],"total":4},"guidelines":[],"source":"Drug Landscape verified database"}