{"disease":{"id":"microcephalic-primordial-dwarfism","name":"microcephalic primordial dwarfism"},"drugs":{"marketed":[],"pipeline":[],"offLabel":[],"totalMarketed":0,"totalPipeline":0},"trials":{"data":[{"nct_id":"NCT04569149","title":"Primordial Dwarfism Registry","phase":"","overall_status":"RECRUITING","enrollment_count":200,"lead_sponsor_name":"Nemours Children's Clinic","has_results":false},{"nct_id":"NCT06111950","title":"Study of the Pathophysiology of RNU4ATAC and RTTN Associated Syndromes","phase":"NA","overall_status":"RECRUITING","enrollment_count":45,"lead_sponsor_name":"Hospices Civils de Lyon","has_results":false}],"total":2},"guidelines":[],"source":"Drug Landscape verified database"}