{"disease":{"id":"metachromatic-leukodystrophy-mld","name":"metachromatic leukodystrophy mld"},"drugs":{"marketed":[],"pipeline":[],"offLabel":[],"totalMarketed":0,"totalPipeline":0},"trials":{"data":[{"nct_id":"NCT03771898","title":"A Study of Intrathecal SHP611 in Children With Metachromatic Leukodystrophy","phase":"PHASE2","overall_status":"ACTIVE_NOT_RECRUITING","enrollment_count":36,"lead_sponsor_name":"Shire","has_results":true},{"nct_id":"NCT01510028","title":"Multicenter Study of HGT-1110 Administered Intrathecally in Children With Metachromatic Leukodystrophy (MLD)","phase":"PHASE1, PHASE2","overall_status":"COMPLETED","enrollment_count":24,"lead_sponsor_name":"Shire","has_results":true},{"nct_id":"NCT01887938","title":"An Efficacy and Safety Study of HGT-1110 in Participants With Metachromatic Leukodystrophy","phase":"PHASE1, PHASE2","overall_status":"ACTIVE_NOT_RECRUITING","enrollment_count":24,"lead_sponsor_name":"Shire","has_results":false},{"nct_id":"NCT00418561","title":"Metazym for the Treatment of Patients With Late Infantile Metachromatic Leukodystrophy (MLD)","phase":"PHASE1","overall_status":"COMPLETED","enrollment_count":13,"lead_sponsor_name":"Shire","has_results":true},{"nct_id":"NCT07046338","title":"Lentiviral Hematopoietic Stem Cell Gene Therapy for MLD","phase":"NA","overall_status":"RECRUITING","enrollment_count":10,"lead_sponsor_name":"Shenzhen Geno-Immune Medical Institute","has_results":false},{"nct_id":"NCT03725670","title":"Direct Lentiviral Injection Gene Therapy for MLD","phase":"NA","overall_status":"RECRUITING","enrollment_count":10,"lead_sponsor_name":"Shenzhen Geno-Immune Medical Institute","has_results":false},{"nct_id":"NCT01963650","title":"Natural History Study of Children With Metachromatic Leukodystrophy","phase":"","overall_status":"TERMINATED","enrollment_count":1,"lead_sponsor_name":"Shire","has_results":false},{"nct_id":"NCT05755568","title":"A Study to Learn About Metachromatic Leukodystrophy (MLD) in Children in Spain","phase":"","overall_status":"WITHDRAWN","enrollment_count":0,"lead_sponsor_name":"Takeda","has_results":false}],"total":8},"guidelines":[],"source":"Drug Landscape verified database"}