{"disease":{"id":"longchain-3-hydroxy-acyl-coa-dehydrogenase-lchad-deficiency","name":"longchain 3 hydroxy acyl coa dehydrogenase lchad deficiency"},"drugs":{"marketed":[],"pipeline":[],"offLabel":[],"totalMarketed":0,"totalPipeline":0},"trials":{"data":[{"nct_id":"NCT01886378","title":"A Study of UX007 (Triheptanoin) in Participants With Long-Chain Fatty Acid Oxidation Disorders (LC-FAOD)","phase":"PHASE2","overall_status":"COMPLETED","enrollment_count":29,"lead_sponsor_name":"Ultragenyx Pharmaceutical Inc","has_results":true}],"total":1},"guidelines":[],"source":"Drug Landscape verified database"}