{"disease":{"id":"leber-congenital-amaurosis-lca","name":"leber congenital amaurosis lca"},"drugs":{"marketed":[],"pipeline":[],"offLabel":[],"totalMarketed":0,"totalPipeline":0},"trials":{"data":[{"nct_id":"NCT03655223","title":"Early Check: Expanded Screening in Newborns","phase":"","overall_status":"ENROLLING_BY_INVITATION","enrollment_count":30000,"lead_sponsor_name":"RTI International","has_results":false},{"nct_id":"NCT07026565","title":"Psychotherapy Group for Parents of Children With LCA","phase":"NA","overall_status":"NOT_YET_RECRUITING","enrollment_count":40,"lead_sponsor_name":"Instituto de Genética Ocular","has_results":false},{"nct_id":"NCT03920007","title":"Study of Subretinally Injected ATSN-101 Administered in Patients With Leber Congenital Amaurosis Caused by Biallelic Mutations in GUCY2D","phase":"PHASE1, PHASE2","overall_status":"ACTIVE_NOT_RECRUITING","enrollment_count":15,"lead_sponsor_name":"Atsena Therapeutics Inc.","has_results":false}],"total":3},"guidelines":[],"source":"Drug Landscape verified database"}