{"disease":{"id":"kabuki-syndrome-1","name":"kabuki syndrome 1"},"drugs":{"marketed":[],"pipeline":[],"offLabel":[],"totalMarketed":0,"totalPipeline":0},"trials":{"data":[{"nct_id":"NCT03855631","title":"Exploiting Epigenome Editing in Kabuki Syndrome: a New Route Towards Gene Therapy for Rare Genetic Disorders","phase":"","overall_status":"COMPLETED","enrollment_count":8,"lead_sponsor_name":"University Hospital, Montpellier","has_results":false}],"total":1},"guidelines":[],"source":"Drug Landscape verified database"}