{"disease":{"id":"hyperphenylalaninemia-hpa","name":"hyperphenylalaninemia hpa"},"drugs":{"marketed":[{"drug_id":"sepiapterin","indication_name":"hyperphenylalaninemia (HPA)","indication_type":"approved","phase":null,"line_of_therapy":null,"is_primary_indication":false,"pivotal_trial_result":null,"pivotal_trial_p_value":null,"patient_population":null,"brand_name":"Sephience","generic_name":"SEPIAPTERIN","company_name":"Ptc Therap","drug_phase":"marketed","molecular_target":"","drug_class":"","quality_score":46,"revenue":null,"mechanism":"Sephience works by replenishing tetrahydrobiopterin (BH4), a critical cofactor for amino acid metabolism."}],"pipeline":[],"offLabel":[],"totalMarketed":1,"totalPipeline":0},"trials":{"data":[],"total":0},"guidelines":[],"source":"Drug Landscape verified database"}