{"disease":{"id":"gaucher-disease-type-3","name":"gaucher disease type 3"},"drugs":{"marketed":[],"pipeline":[],"offLabel":[],"totalMarketed":0,"totalPipeline":0},"trials":{"data":[{"nct_id":"NCT05687474","title":"Baby Detect : Genomic Newborn Screening","phase":"","overall_status":"COMPLETED","enrollment_count":6824,"lead_sponsor_name":"Centre Hospitalier Universitaire de Liege","has_results":false},{"nct_id":"NCT06627543","title":"Effect of Enzyme Replacement Therapy on Cardiac Function in Children With Gaucher Disease Type 3","phase":"","overall_status":"ENROLLING_BY_INVITATION","enrollment_count":44,"lead_sponsor_name":"Noha Osman","has_results":false},{"nct_id":"NCT05447494","title":"Phase 1/2 Study of CAN103 in Subjects With Gaucher Disease","phase":"PHASE1, PHASE2","overall_status":"UNKNOWN","enrollment_count":40,"lead_sponsor_name":"CANbridge (Suzhou) Bio-pharma Co., Ltd.","has_results":false},{"nct_id":"NCT03746587","title":"Study of Arimoclomol in Patients Diagnosed With Gaucher Disease Type 1 or 3","phase":"PHASE2","overall_status":"TERMINATED","enrollment_count":39,"lead_sponsor_name":"ZevraDenmark","has_results":false},{"nct_id":"NCT04002830","title":"A Multicenter, Safety and Efficacy Study of Taliglucerase Alfa in Subjects With Type 3 Gaucher Disease","phase":"PHASE4","overall_status":"COMPLETED","enrollment_count":14,"lead_sponsor_name":"Ari Zimran","has_results":true},{"nct_id":"NCT07285369","title":"High-Dose Ambroxol in Pediatric Type III Gaucher Disease (GD3)","phase":"NA","overall_status":"TERMINATED","enrollment_count":12,"lead_sponsor_name":"Agyany Pharma LTD","has_results":false},{"nct_id":"NCT02843035","title":"Venglustat in Combination With Cerezyme in Adult Patients With Gaucher Disease Type 3 With Venglustat Monotherapy Extension","phase":"PHASE2","overall_status":"ACTIVE_NOT_RECRUITING","enrollment_count":12,"lead_sponsor_name":"Genzyme, a Sanofi Company","has_results":false},{"nct_id":"NCT04532047","title":"PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)","phase":"PHASE1","overall_status":"RECRUITING","enrollment_count":10,"lead_sponsor_name":"University of California, San Francisco","has_results":false},{"nct_id":"NCT01685216","title":"Efficacy and Safety Study of Velaglucerase Alfa in Children and Adolescents With Type 3 Gaucher Disease","phase":"PHASE1, PHASE2","overall_status":"COMPLETED","enrollment_count":7,"lead_sponsor_name":"Shire","has_results":true},{"nct_id":"NCT05586243","title":"MAGNETIC RESONANCE SPECTROSCOPY BIOMARKERS IN TYPE 3 GAUCHER DISEASE (GD3)","phase":"","overall_status":"RECRUITING","enrollment_count":5,"lead_sponsor_name":"University of Minnesota","has_results":false}],"total":10},"guidelines":[],"source":"Drug Landscape verified database"}