{"disease":{"id":"cornelia-de-lange-syndrome","name":"cornelia de lange syndrome"},"drugs":{"marketed":[],"pipeline":[],"offLabel":[],"totalMarketed":0,"totalPipeline":0},"trials":{"data":[{"nct_id":"NCT04463316","title":"GROWing Up With Rare GENEtic Syndromes","phase":"","overall_status":"RECRUITING","enrollment_count":600,"lead_sponsor_name":"dr. Laura C. G. de Graaff-Herder","has_results":false},{"nct_id":"NCT05829668","title":"Behavioral Assessment and Treatment of Problem Behavior in Children With Cornelia de Lange Syndrome","phase":"NA","overall_status":"RECRUITING","enrollment_count":20,"lead_sponsor_name":"Hugo W. Moser Research Institute at Kennedy Krieger, Inc.","has_results":false},{"nct_id":"NCT04381897","title":"Use of N-Acetylcysteine in the Treatment of Repetitive and Self-Injurious Behaviors in Cornelia de Lange Syndrome","phase":"PHASE2","overall_status":"NOT_YET_RECRUITING","enrollment_count":10,"lead_sponsor_name":"Johns Hopkins University","has_results":false}],"total":3},"guidelines":[],"source":"Drug Landscape verified database"}