{"disease":{"id":"congenital-muscular-dystrophy-due-to-lamin-a-c-mutation","name":"congenital muscular dystrophy due to lamin a c mutation"},"drugs":{"marketed":[],"pipeline":[],"offLabel":[],"totalMarketed":0,"totalPipeline":0},"trials":{"data":[{"nct_id":"NCT05154851","title":"HBCMD01- Expanded Access for the Treatment of Congenital Muscular Dystrophy.","phase":"","overall_status":"NO_LONGER_AVAILABLE","enrollment_count":null,"lead_sponsor_name":"Hope Biosciences Research Foundation","has_results":false}],"total":1},"guidelines":[],"source":"Drug Landscape verified database"}