{"disease":{"id":"cobalamin-deficiency","name":"Cobalamin deficiency","therapeutic_area":"","data":{},"enrichment_level":0,"last_enriched_at":null,"visit_count":0,"created_at":"2026-04-19T18:31:21.150Z","updated_at":"2026-04-19T18:39:44.960Z","meddra_pt":null,"meddra_code":null,"icd10_codes":null,"synonyms":[],"prevalence_global":null,"prevalence_us":null,"marketed_drug_count":9,"pipeline_drug_count":0,"trial_count":0},"drugs":{"marketed":[{"drug_id":"cyanocobalamin","indication_name":"Cobalamin deficiency","indication_type":"approved","phase":null,"line_of_therapy":null,"is_primary_indication":false,"pivotal_trial_result":null,"pivotal_trial_p_value":null,"patient_population":null,"brand_name":"Rubramin Pc","generic_name":"CYANOCOBALAMIN","company_name":"","drug_phase":"marketed","molecular_target":"Cob(I)yrinic acid a,c-diamide adenosyltransferase, mitochondrial","drug_class":"Vitamin C [EPC]","quality_score":45,"revenue":null,"mechanism":""},{"drug_id":"chlorazanil","indication_name":"Cobalamin deficiency","indication_type":"approved","phase":null,"line_of_therapy":null,"is_primary_indication":false,"pivotal_trial_result":null,"pivotal_trial_p_value":null,"patient_population":null,"brand_name":"Orpizin","generic_name":"CHLORAZANIL","company_name":"","drug_phase":"phase_2","molecular_target":"","drug_class":"","quality_score":null,"revenue":null,"mechanism":"Orpizin works by inhibiting the breakdown of Cobalamin, allowing it to be absorbed and utilized by the body."},{"drug_id":"hydroxycobalamin","indication_name":"Cobalamin deficiency","indication_type":"approved","phase":null,"line_of_therapy":null,"is_primary_indication":false,"pivotal_trial_result":null,"pivotal_trial_p_value":null,"patient_population":null,"brand_name":null,"generic_name":"Hydroxycobalamin","company_name":"Christian Medical College, Vellore, India","drug_phase":"marketed","molecular_target":"","drug_class":"","quality_score":15,"revenue":null,"mechanism":null},{"drug_id":"cobalamin","indication_name":"Cobalamin deficiency","indication_type":"approved","phase":null,"line_of_therapy":null,"is_primary_indication":false,"pivotal_trial_result":null,"pivotal_trial_p_value":null,"patient_population":null,"brand_name":null,"generic_name":"COBALAMIN","company_name":"","drug_phase":"marketed","molecular_target":"","drug_class":"Vitamin C [EPC]","quality_score":34,"revenue":null,"mechanism":""},{"drug_id":"amanozine","indication_name":"Cobalamin deficiency","indication_type":"approved","phase":null,"line_of_therapy":null,"is_primary_indication":false,"pivotal_trial_result":null,"pivotal_trial_p_value":null,"patient_population":null,"brand_name":"Urofort","generic_name":"AMANOZINE","company_name":"","drug_phase":"phase_2","molecular_target":"","drug_class":"","quality_score":null,"revenue":null,"mechanism":"Urofort works by providing a source of Cobalamin to the body, helping to address deficiencies and prevent related conditions."},{"drug_id":"cyanocobalamin-57co","indication_name":"Cobalamin deficiency","indication_type":"approved","phase":null,"line_of_therapy":null,"is_primary_indication":false,"pivotal_trial_result":null,"pivotal_trial_p_value":null,"patient_population":null,"brand_name":"Cyanocobalamin Co 57","generic_name":"cyanocobalamin (57Co)","company_name":"Mallinckrodt","drug_phase":"marketed","molecular_target":"Cob(I)yrinic acid a,c-diamide adenosyltransferase, mitochondrial, Methionine synthase, Methionine synthase reductase","drug_class":"Radioactive Diagnostic Agent","quality_score":24,"revenue":null,"mechanism":""},{"drug_id":"hydroxocobalamin","indication_name":"Cobalamin deficiency","indication_type":"approved","phase":null,"line_of_therapy":null,"is_primary_indication":false,"pivotal_trial_result":null,"pivotal_trial_p_value":null,"patient_population":null,"brand_name":"Cyanokit","generic_name":"HYDROXOCOBALAMIN","company_name":"Btg Intl","drug_phase":"marketed","molecular_target":"","drug_class":"Antidote","quality_score":10,"revenue":null,"mechanism":""},{"drug_id":"thiamine","indication_name":"Cobalamin deficiency","indication_type":"approved","phase":null,"line_of_therapy":null,"is_primary_indication":false,"pivotal_trial_result":null,"pivotal_trial_p_value":null,"patient_population":null,"brand_name":"Thiamine Hydrochloride","generic_name":"THIAMINE","company_name":"Pfizer","drug_phase":"marketed","molecular_target":"Heat shock protein HSP 90-alpha","drug_class":"thiamine (vit B1)","quality_score":40,"revenue":null,"mechanism":""},{"drug_id":"thiamin","indication_name":"Cobalamin deficiency","indication_type":"approved","phase":null,"line_of_therapy":null,"is_primary_indication":false,"pivotal_trial_result":null,"pivotal_trial_p_value":null,"patient_population":null,"brand_name":null,"generic_name":"Thiamin","company_name":"Hospital Sao Domingos","drug_phase":"marketed","molecular_target":"Thiamin pyrophosphokinase 1, Thiamine transporter 1, Thiamine-triphosphatase","drug_class":"","quality_score":null,"revenue":null,"mechanism":null}],"pipeline":[],"offLabel":[],"totalMarketed":9,"totalPipeline":0},"trials":{"data":[{"nct_id":"NCT03655223","title":"Early Check: Expanded Screening in Newborns","phase":"","overall_status":"ENROLLING_BY_INVITATION","enrollment_count":30000,"lead_sponsor_name":"RTI International","has_results":false},{"nct_id":"NCT05687474","title":"Baby Detect : Genomic Newborn Screening","phase":"","overall_status":"COMPLETED","enrollment_count":6824,"lead_sponsor_name":"Centre Hospitalier Universitaire de Liege","has_results":false}],"total":2},"guidelines":[],"source":"Drug Landscape verified database"}