{"disease":{"id":"classic-galactosemia","name":"classic galactosemia"},"drugs":{"marketed":[],"pipeline":[],"offLabel":[],"totalMarketed":0,"totalPipeline":0},"trials":{"data":[{"nct_id":"NCT03838016","title":"Preventing Speech and Language Disorders in Children With Classic Galactosemia","phase":"EARLY_PHASE1","overall_status":"COMPLETED","enrollment_count":285,"lead_sponsor_name":"Arizona State University","has_results":false},{"nct_id":"NCT04117711","title":"Safety and Pharmacokinetics of AT-007 in Healthy Subjects and in Adult Subjects With Classic Galactosemia","phase":"PHASE1, PHASE2","overall_status":"COMPLETED","enrollment_count":114,"lead_sponsor_name":"Applied Therapeutics, Inc.","has_results":true},{"nct_id":"NCT04902781","title":"Clinical Benefit, Safety, PK and PD Study of AT-007 in Pediatric Subjects With Classic Galactosemia","phase":"PHASE2, PHASE3","overall_status":"COMPLETED","enrollment_count":47,"lead_sponsor_name":"Applied Therapeutics, Inc.","has_results":false},{"nct_id":"NCT03580122","title":"The Effect of Arginine on Classic Galactosemia","phase":"PHASE2","overall_status":"COMPLETED","enrollment_count":4,"lead_sponsor_name":"Academisch Ziekenhuis Maastricht","has_results":false}],"total":4},"guidelines":[],"source":"Drug Landscape verified database"}